Studienbeschreibung
TitelMigalastat
KurztitelMigalastat Beob. Stu
Allgemeinverständliche KurzbeschreibungThe objective of the study is to generate long term data on treatment with Migalastat under "real world" conditions. The selection of patients will be based on the SmPC/Fachinformation. The treatment duration/patient will be 2 years. All patients will be followed-up by the German Fabry expert centers that are listed below.
Wissenschaftliche KurzbeschreibungGerman observational multicenter study of patients with Fabry disease under chaperone therapy with Migalastat-HCl.
Studienstart16.09.2020
Untersuchte Krankheit, Gesundheitsproblem
ICD-Code- E75.2 - Sonstige Sphingolipidosen
Einschlusskriterien
Alter18 - 99
GeschlechtAlle
Weitere EinschlusskriterienThe objective of the study is to generate long term data on treatment with Migalastat under "real world" conditions. The selection of patients will be based on the SmPC/Fachinformation. The treatment duration/patient will be 2 years. All patients will be followed-up by the German Fabry expert centers that are listed below.
Ausschlusskriterien
The objective of the study is to generate long term data on treatment with Migalastat under "real world" conditions. The selection of patients will be based on the SmPC/Fachinformation. The treatment duration/patient will be 2 years. All patients will be followed-up by the German Fabry expert centers that are listed below.
Charakteristika
StudientypNicht-interventionell
StudienphaseNicht zutreffend